Development and chronology of the document The drafting of this document was curated by the working group (GDL) Gene therapy of the Ace, chaired by Angiola Rocino, president of Aice for the three-year period 2020-2023, coordinated by Flora Peyvandi and Giancarlo Castaman and made up of: Andrea Buzzi, Enrico Ferri Grazzi (patient representatives), Maria Basso, Paolo Angelo Cristofaro, Raimondo De Cristofaro, Giovanni di Minno, Matteo Nicola Dario di Minno, Isabella Garagiola, Alessandro Gringeri, Veronica Grippa, Vincenzo La Mura, Marzia Leotta, Corrado Lodigiani, Mariasanta Napolitano, Mirko Pinotti, Rita Carlotta Santoro,Paolo Simioni,Annarita Tagliaferri,Armando Tripodi和Ezio Zanon。Development and chronology of the document The drafting of this document was curated by the working group (GDL) Gene therapy of the Ace, chaired by Angiola Rocino, president of Aice for the three-year period 2020-2023, coordinated by Flora Peyvandi and Giancarlo Castaman and made up of: Andrea Buzzi, Enrico Ferri Grazzi (patient representatives), Maria Basso, Paolo Angelo Cristofaro, Raimondo De Cristofaro, Giovanni di Minno, Matteo Nicola Dario di Minno, Isabella Garagiola, Alessandro Gringeri, Veronica Grippa, Vincenzo La Mura, Marzia Leotta, Corrado Lodigiani, Mariasanta Napolitano, Mirko Pinotti, Rita Carlotta Santoro,Paolo Simioni,Annarita Tagliaferri,Armando Tripodi和Ezio Zanon。