2.11.6。strimvelis-自体CD34+富集的细胞馏分,其中包含用逆转录病毒载体转导的CD34+细胞,该逆转录病毒载体编码为人ADA cDNA序列 - orphan -emea/h/c/c/003854/ii/ii/ii/ii/ii/ii/ii/0040 .....................................................................................................................................................................................................................................................................................................................