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“这样的研究对于一般和NPC1患者的基因疗法治疗的分娩策略非常重要,例如确定试验的入学标准,治疗方案是否需要减轻先前存在的NAB,以及在生活过程中NAB的发展可能会影响Hull of Human Gene edior of Munly Gention of Munly Gention of Hull of Munly Gention of Hull of Munly Gention of Hull of Hull of Hull of Hull of Hull of Human Gention for Human Gention of Hull of Hull of Hull of Hull of Hull of Hull of Hull of Hull of Hull of the the。马萨诸塞州chan

评估Niemann-Pick疾病个体中和抗体的患病率

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