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造血干细胞的碱基编辑挽救了小鼠的镰状细胞病 Gregory A. Newby 1,2,3,12 , Jonathan S. Yen 4,12 *, Kaitly J. Woodard 4,12 , Thiyagaraj Mayuranathan 4,12 , Cicera R. Lazzarotto 4 , Yichao Li 4 , Heather Sheppard-Tillman 5 , Shaina N. Porter 5 , Yu Yao 4 , Kalin Mayberry 4 , Kelcee A. Everette 1,2,3 , Yoonjeong Jang 4 , Christopher J. Podracky 1,2,3 , Elizabeth Thaman 7 , Christophe Lechauve 4 , Akshay Sharma 8 , Jordana M. Henderson 9 , Michelle F. Richter 1,2,3 , Kevin T. Zhao 1,2,3 , Shannon M. Miller 1,2,3 , Tina Wang 1,2,3 , Luke W. Koblan 1,2,3 , Anton P. McCaffrey 9 , John F. Tisdale 10 , Theodosia A. Kalfa 6,11 , Shondra M. Pruett-Miller 5 , Shengdar Q. Tsai 4 , Mitchell J. Weiss 4 *, David R. Liu 1,2,3 *

Makassar Manucript v121.drl - 哈佛 DASH

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